Gene therapy that led to boy’s death had limited efficacy
Therapy pioneered by biotechnology Chinese firm HuidaGene showed promise in animals but caused a fatal reaction in a child.
Results from the first human trial of an experimental gene-editing therapy for Duchenne muscular dystrophy (DMD), in which a young Chinese boy died, have been published1. Although the trial provides evidence that the treatment developed by HuidaGene,... [5116 chars]
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